RGRonald G CrystalJWJonathan W WeinsaftSMStephen M. KaminskyRJRobert J. KanerASAbraham Sanders+4 more →
JAMA cardiology · 2026
Research area
Gene & Cell Therapy
Translational research on therapeutic delivery of genetic material and cellular constructs for disease treatment including AAV-mediated gene delivery, CAR-T cell therapy, and pharmacological chaperone approaches. Covers vector design, safety characterization, and preclinical and clinical development of gene and cell-based therapeutics.
Scholars in this area
View all 193 scholars →- George CoukosWalter B. Wriston Professor of Pancreatic Cancer Research I
- Adoptive T Cell Transfer Therapies
- CAR T Cell Engineering & Outcomes
- iPSC Derivation & CRISPR Disease Modeling
George CoukosWalter B. Wriston Professor of Pancreatic Cancer Research I- Adoptive T Cell Transfer Therapies
- CAR T Cell Engineering & Outcomes
- iPSC Derivation & CRISPR Disease Modeling
- Szilard KissBob and Dolores Hope - Robert M. Ellsworth, M.D. Distinguished Professor in Ophthalmology
- Ocular & Retinal Gene Therapy
- AAV Therapy for Neurological Disorders
- Adoptive T Cell Transfer Therapies
Szilard KissBob and Dolores Hope - Robert M. Ellsworth, M.D. Distinguished Professor in Ophthalmology- Ocular & Retinal Gene Therapy
- AAV Therapy for Neurological Disorders
- Adoptive T Cell Transfer Therapies
- Dolan SondhiProfessor of Research in Genetic Medicine
- AAV Therapy for Neurological Disorders
- AAV Vector Engineering & Safety
- Ocular & Retinal Gene Therapy
Dolan SondhiProfessor of Research in Genetic Medicine- AAV Therapy for Neurological Disorders
- AAV Vector Engineering & Safety
- Ocular & Retinal Gene Therapy
Spotlight
Spotlight page 1 of 3
American journal of hematology · 2026
Nature biotechnology · 2020