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Scholars/Ronald G Crystal, MD/Co-authored with mentees

Co-authored publications with mentees

Ronald G Crystal, MD · 10 publications across 9 mentees

PhD mentee

Consequences of human genetic variations in KIAA0319L, encoding adeno-associated virus receptor, on AAV-mediated gene transfer.
Molecular therapy. Advances · 2026
RGRonald G CrystalJVJenifer VasquezMRMahboubeh Rahmati Rostami PLPhilip L. Leopold
PMID: 42137583PMCID: PMC13148924DOI
With Jenifer Vasquez · Physiology, Biophysics & Systems Biology (PhD) · Class of 2026
Predicted deleterious variants in the human genome relevant to gene therapy with adeno-associated virus vectors.
Molecular therapy. Methods & clinical development · 2023
RGRonald G CrystalJVJenifer VasquezMRMahboubeh Rahmati Rostami PLPhilip L. Leopold MDMiguel de Mulder Rougvie+3 more →
PMID: 38089635PMCID: PMC10711236DOI4 citations
With Jenifer Vasquez · Physiology, Biophysics & Systems Biology (PhD) · Class of 2026

Postdoc mentee

Vectorized Human Antibody-Mediated Anti-Eosinophil Gene Therapy.
Human gene therapy · 2024
RGRonald G CrystalMGMaria GioulvanidouILIvo LorenzKMKatie M StilesOPOdelya Pagovich+3 more →
PMID: 39725494PMCID: PMC11839538DOI
With Maria Gioulvanidou · Postdoc mentee
Suppression of CNS APOE4 Expression by miRNAs Delivered by the S2 AAVrh.10 Capsid-Modified AAV Vector.
Human gene therapy · 2024
RGRonald G CrystalSASlawomir AndrzejewskiKMKatie M StilesNRNeil R. Hackett
PMID: 39318239DOI5 citations
With Slawomir Andrzejewski · Postdoc mentee
Identification of Safe and Effective Intravenous Dose of AAVrh.10hFXN to Treat the Cardiac Manifestations of Friedreich's Ataxia.
Human gene therapy · 2023
RGRonald G CrystalCMCarlos Munoz-ZuluagaMGMonica GertzSMStephen M. Kaminsky+2 more →DSDolan Sondhi
PMID: 37166361PMCID: PMC10354731DOI17 citations
With Carlos Munoz Zuluaga · Postdoc mentee
Identification of Safe and Effective Intravenous Dose of AAVrh.10hFXN to Treat the Cardiac Manifestations of Friedreich's Ataxia.
Human gene therapy · 2023
RGRonald G CrystalMGMonica GertzCMCarlos Munoz-ZuluagaSMStephen M. Kaminsky+2 more →DSDolan Sondhi
PMID: 37166361PMCID: PMC10354731DOI17 citations
With Monica Gertz · Postdoc mentee
Safety of Intravenous Administration of an AAV8 Vector Coding for an Oxidation-Resistant Human α1-Antitrypsin for the Treatment of α1-Antitrypsin Deficiency.
Human gene therapy · 2023
RGRonald G CrystalCMCarlos Munoz-ZuluagaSMStephen M. Kaminsky MRMahboubeh Rahmati Rostami DSDolan Sondhi
PMID: 36606685PMCID: PMC9963503DOI8 citations
With Carlos Munoz Zuluaga · Postdoc mentee
Can gene therapy be used to prevent cancer? Gene therapy for aldehyde dehydrogenase 2 deficiency.
Cancer gene therapy · 2021
RGRonald G CrystalCMCarlos Munoz-ZuluagaRARachel A MontelKMKatie M Stiles
PMID: 34799722PMCID: PMC9117562DOI9 citations
With Carlos Munoz Zuluaga · Postdoc mentee
Can gene therapy be used to prevent cancer? Gene therapy for aldehyde dehydrogenase 2 deficiency.
Cancer gene therapy · 2021
RGRonald G CrystalRARachel A MontelCMCarlos Munoz-ZuluagaKMKatie M Stiles
PMID: 34799722PMCID: PMC9117562DOI9 citations
With Rachel Montel · Postdoc mentee
CREB-dependent LPA-induced signaling initiates a pro-fibrotic feedback loop between small airway basal cells and fibroblasts.
Respiratory research · 2021
RGRonald G CrystalSNShyam NathanHZHaijun Zhang PLPhilip L. Leopold
PMID: 33794877PMCID: PMC8015171DOI10 citations
With Shyam Nathan · Postdoc mentee
Gene therapy for alpha 1-antitrypsin deficiency with an oxidant-resistant human alpha 1-antitrypsin.
JCI insight · 2020
RGRonald G CrystalMLMeredith L SosulskiKMKatie M StilesSMStephen M. Kaminsky
PMID: 32759494PMCID: PMC7455074DOI17 citations
With Meredith Sosulski · Postdoc mentee
Single-Cell Transcriptome Analysis of Mouse Liver Cell-Specific Tropism and Transcriptional Dysregulation Following Intravenous Administration of AAVrh.10 Vectors.
Human gene therapy · 2020
RGRonald G CrystalDZDetu ZhuMRMahboubeh Rahmati Rostami PLPhilip L. Leopold
PMID: 32143547PMCID: PMC7232697DOI15 citations
With Detu Zhu · Postdoc mentee