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Ronald G Crystal, MD
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Co-authored with Carlos Munoz Zuluaga
Co-authored publications
Ronald G Crystal, MD and Carlos Munoz Zuluaga · 3 publications
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Identification of Safe and Effective Intravenous Dose of AAVrh.10hFXN to Treat the Cardiac Manifestations of Friedreich's Ataxia.
Human gene therapy
· 2023
RG
Ronald G Crystal
CM
Carlos Munoz-Zuluaga
MG
Monica Gertz
SM
Stephen M. Kaminsky
+2 more →
DS
Dolan Sondhi
PMID:
37166361
·
PMCID:
PMC10354731
·
DOI
·
17 citations
·
Abstract
Safety of Intravenous Administration of an AAV8 Vector Coding for an Oxidation-Resistant Human α1-Antitrypsin for the Treatment of α1-Antitrypsin Deficiency.
Human gene therapy
· 2023
RG
Ronald G Crystal
CM
Carlos Munoz-Zuluaga
SM
Stephen M. Kaminsky
MR
Mahboubeh Rahmati Rostami
DS
Dolan Sondhi
PMID:
36606685
·
PMCID:
PMC9963503
·
DOI
·
8 citations
·
Abstract
Can gene therapy be used to prevent cancer? Gene therapy for aldehyde dehydrogenase 2 deficiency.
Cancer gene therapy
· 2021
RG
Ronald G Crystal
CM
Carlos Munoz-Zuluaga
RA
Rachel A Montel
KM
Katie M Stiles
PMID:
34799722
·
PMCID:
PMC9117562
·
DOI
·
9 citations
·
Abstract